CureDuchenne is a national nonprofit that raises awareness and funds research to find a cure for Duchenne muscular dystrophy.
Duchenne is an inherited genetic disease with no treatment or cure. Duchenne causes progressive muscle degeneration, often leaving patients wheelchair bound by their mid-teens. The average life expectancy of someone with Duchenne is their mid-20s.
The organization was founded by Paul and Debra Miller in 2004 after their son was diagnosed with Duchenne. At the time, there was not an organization focused exclusively on finding a cure for Duchenne. Today, the world’s leading scientists are working with CureDuchenne to help determine the most viable research projects and to accelerate the clinical trial process. To date, seven research projects that CureDuchenne has funded have advanced into human clinical trials Three of these pharmaceutical treatments could be approved by the FDA within the next year.
These treatments may lessen the effects of the disease with certain mutations of Duchenne, but there is still much work to be done to find a cure. Our goal is to halt the progress of the disease by bringing potential life-saving drugs to help this generation of Duchenne boys.